Genetic diseases result, at least in part, from changes in our DNA .
A change in a single letter in the genetic code can cause debilitating, life-changing consequences for children and families.
CMRI scientists are tackling genetic diseases through Gene Therapy – the ‘medicine of the future’, which can one day provide cures for countless children like Mollyjane. Her genetic disease (CACT deficiency) threatens her life every day.
Your support today of CMRI’s gene therapy program at this crucial time will enable our research to develop cures for many childhood genetic diseases.
70 cents from every dollar donated goes directly to research.